Syndeo Life
Syndeo Life
Categories
Biotechnology
About
a Baltimore, Maryland-based biotechnology company and Johns Hopkins University spinout dedicated to developing pioneering gene therapies and biomarkers for neurodegenerative diseases driven by TDP-43 dysfunction. The company’s flagship program, AAV9-CTR, is engineered as a one-time intrathecal gene therapy designed to rescue transcriptome-wide splicing errors and restore normal cellular function across hundreds of targets, initially focusing on amyotrophic lateral sclerosis (ALS) with future plans to expand into frontotemporal dementia (FTD) and Alzheimer’s disease.
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Life Sciences Pennsylvania was founded in 1989 by a biotech scientist at Penn State University. Today it has grown to represent the entire life sciences industry – biotechnology and diagnostic companies, medical device companies, pharmaceutical companies, investment organizations, research institutions, and myriad service industries that support the life sciences in Pennsylvania.